A groundbreaking gene therapy developed through a UCLA-led clinical trial has received approval from the U.S. Food and Drug ...
New results from a clinical trial show promising outcomes for a gene-edited treatment for severe sickle cell disease, a ...
A child who feels tired often, has repeated hospital visits, or unexplained pain may point to conditions like Sickle Cell ...
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Mother whose baby was diagnosed with rare blood condition urges people to join stem cell register
Closer to the truth? In this gripping documentary, a forensic scientist and pathologist reinvestigate two murder-suicides ...
Ronnie, from Merseyside, had just started crawling when his mother Laura noticed he was bruising more.
Alicia and Jon Langenhop's three children were each diagnosed with a rare disorder. A clinical trial was "a no-brainer." ...
Families across Central Texas can now access lifesaving pediatric bone marrow transplants, which has eliminated the need to travel for advanced cancer care, Dell Children's physicians said.
Diagnosed with a rare blood condition a week before his first birthday, Ronnie's mother, Laura, first noticed increased ...
An effort is underway to find a bone marrow match for 11-year-old Cate Hargett, who suffers from bone marrow failure.
The (ASH) released guidelines on the diagnosis and management of severe acquired aplastic anemia, a rare and ...
Noah had always been a happy and healthy child, but that all changed in July 2018 when he woke up with severe leg and ...
Chantez Sanford Jr., 24, of Southfield, says his life has been transformed after undergoing Lyfgenia gene therapy at Children ...
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